Muscular Dystrophy News
February 12, 2025
Top Headlines
Dec. 31, 2024 — A groundbreaking study has shed light on the complex interactions between dystrophin, a protein critical to muscle stability, and its partner protein, dystrobrevin, offering new pathways for ...
Dec. 16, 2024 — A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. Researchers have discovered that an experimental compound called K884 can boost the natural repair abilities ...
Nov. 14, 2024 — StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal ...
Oct. 24, 2024 — A new mouse model mimicking the liver symptoms of myotonic dystrophy type 1 -- the most prevalent form of adult-onset muscular dystrophy -- provides insight into why patients develop fatty liver disease and display hypersensitivity to medications, ...
Latest Headlines
updated 10:49pm EST
July 24, 2024 — Researchers have made a significant breakthrough in developing a new gene therapy approach that restores full-length dystrophin protein, which could lead to new treatments for people with Duchenne ...
July 22, 2024 — In a finding that opens the door to the development of targeted therapies for various muscle disorders, newly published research identifies key mechanisms of skeletal muscle regeneration and growth ...
July 17, 2024 — A new gene therapy treatment for Duchenne muscular dystrophy (DMD) shows promise of not only arresting the decline of the muscles of those affected by this inherited genetic disease, but perhaps, in ...
Mar. 6, 2024 — A specific gene may play a key role in new treatments that prevent muscle in the body from breaking down in serious muscle diseases, muscular ...
Jan. 2, 2024 — New research has identified the specific biological mechanism behind the muscle dysfunction found in myotonic dystrophy type 1 (DM1) and further ...
Aug. 24, 2023 — Duchenne muscular dystrophy (DMD) is a muscle degeneration disorder caused by mutations affecting the dystrophin gene. Researchers show how a dual ...
Aug. 16, 2023 — A new method allows large quantities of muscle stem cells to be safely obtained in cell culture. This provides a potential for treating patients with muscle diseases -- and for those who would like ...
July 31, 2023 — The research team administered AP39 to some worms from birth, and to others after reaching adulthood. They found that this compound improved the ...
May 24, 2023 — A research team has discovered that by manipulating a certain protein in the immune system they can slow down disease progression and improve muscle function in Duchenne muscular ...
Apr. 13, 2023 — Investigators recently used a targeted drug to restore muscle strength and correct myotonia in mice with myotonic ...
Earlier Headlines
Feb. 27, 2023 — New research has uncovered a novel link between the Duchenne muscular dystrophy (DMD) gene and ...
Dec. 19, 2022 — Therapies to target neuromuscular disorders affecting million of people worldwide are on the horizon thanks to research at the Montreal Clinical Research Institute of Montreal. Fusion of myoblasts, ...
Dec. 12, 2022 — Fukuyama congenital muscular dystrophy (FCMD) is the second most common form of childhood muscular dystrophy in Japan. The disease manifests itself in the form of a severe neuromuscular disorder. One ...
Sep. 13, 2022 — Researchers report that an experimental drug first developed to treat kidney disease prolongs survival and improves muscle function in mice genetically engineered to develop a severe form of Duchenne ...
May 4, 2022 — New research recommends daily steroid doses for children with Duchenne muscular dystrophy, marking a significant change in how the disease is ...
Apr. 20, 2022 — In proof-of-concept experiments, scientists say they have successfully cultivated human muscle stem cells capable of renewing themselves and repairing muscle tissue damage in mice, potentially ...
Apr. 13, 2022 — A cell therapy stabilizes weakened muscles -- including the heart muscle -- in Duchenne muscular dystrophy patients, a new study ...
Apr. 11, 2022 — Patients who took part in the study saw a 1.6-kilogram increase in their muscle mass and a two per cent reduction of body fat. They were also able to walk an extra 47 meters in six minutes, when ...
Apr. 1, 2022 — Obese mice that were fed a high-fat diet and that received prednisone one time per week had improved exercise endurance, got stronger, increased their lean body mass and lost weight, reports a new ...
Mar. 24, 2022 — A new study using neuromuscular electrical stimulation (NMES) in zebrafish found that certain activities may help strengthen muscles affected by Duchenne muscular dystrophy, a severe type of muscular ...
Mar. 18, 2022 — Tracing the impact of a single protein, Piezo1, researchers found that restoring it in muscles affected by Duchenne muscular dystrophy could improve their ability to heal ...
Mar. 10, 2022 — A recent clinical trial has shown that cellular therapy is safe and effective in stopping the deterioration of upper limb and heart functions in patients with late-stage Duchenne muscular ...
Feb. 23, 2022 — A new 'cocktail' drug under development could provide an effective and economical treatment to lessen symptoms for up to 45 per cent of patients with Duchenne muscular dystrophy (DMD), a ...
Feb. 18, 2022 — Latest advance in chronopharmacology, based on mouse models, suggests that time-of-day matters when using steroids to treat muscle ...