Muscular Dystrophy News
May 16, 2025
Top Headlines
May 14, 2025 — Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene ...
Apr. 8, 2025 — A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective ...
Mar. 26, 2025 — A team has discovered a possible therapeutic approach to repair injured muscles either from aging or degenerative muscle ...
Mar. 18, 2025 — Researchers focused on Myotonic Dystrophy 1 heart problems are testing a novel approach to restore normal ...
Latest Headlines
updated 10:43pm EDT
Mar. 5, 2025 — Researchers combined advanced imaging techniques and theoretical physics to observe and explain how nanoclusters of the protein emerin form inside living cells. The study uncovers the molecular ...
Dec. 31, 2024 — A groundbreaking study has shed light on the complex interactions between dystrophin, a protein critical to muscle stability, and its partner ...
Dec. 16, 2024 — A novel drug holds promise for treating Duchenne muscular dystrophy (DMD), a rare genetic disorder that causes severe muscle degeneration. Researchers have discovered that an experimental compound ...
Nov. 14, 2024 — StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal ...
Oct. 24, 2024 — A new mouse model mimicking the liver symptoms of myotonic dystrophy type 1 -- the most prevalent form of adult-onset muscular dystrophy -- provides insight into why patients develop fatty liver ...
July 24, 2024 — Researchers have made a significant breakthrough in developing a new gene therapy approach that restores full-length dystrophin protein, which could lead to new treatments for people with Duchenne ...
July 22, 2024 — In a finding that opens the door to the development of targeted therapies for various muscle disorders, newly published research identifies key mechanisms of skeletal muscle regeneration and growth ...
July 17, 2024 — A new gene therapy treatment for Duchenne muscular dystrophy (DMD) shows promise of not only arresting the decline of the muscles of those affected by this inherited genetic disease, but perhaps, in ...
Mar. 6, 2024 — A specific gene may play a key role in new treatments that prevent muscle in the body from breaking down in serious muscle diseases, muscular ...
Jan. 2, 2024 — New research has identified the specific biological mechanism behind the muscle dysfunction found in myotonic dystrophy type 1 (DM1) and further ...
Earlier Headlines
Aug. 24, 2023 — Duchenne muscular dystrophy (DMD) is a muscle degeneration disorder caused by mutations affecting the dystrophin gene. Researchers show how a dual CRISPR RNA method restored dystrophin protein ...
Aug. 16, 2023 — A new method allows large quantities of muscle stem cells to be safely obtained in cell culture. This provides a potential for treating patients with muscle diseases -- and for those who would like ...
July 31, 2023 — The research team administered AP39 to some worms from birth, and to others after reaching adulthood. They found that this compound improved the integrity of mitochondria -- the 'power ...
May 24, 2023 — A research team has discovered that by manipulating a certain protein in the immune system they can slow down disease progression and improve muscle function in Duchenne muscular ...
Apr. 13, 2023 — Investigators recently used a targeted drug to restore muscle strength and correct myotonia in mice with myotonic ...
Feb. 27, 2023 — New research has uncovered a novel link between the Duchenne muscular dystrophy (DMD) gene and ...
Dec. 19, 2022 — Therapies to target neuromuscular disorders affecting million of people worldwide are on the horizon thanks to research at the Montreal Clinical Research Institute of Montreal. Fusion of myoblasts, ...
Dec. 12, 2022 — Fukuyama congenital muscular dystrophy (FCMD) is the second most common form of childhood muscular dystrophy in Japan. The disease manifests itself in the form of a severe neuromuscular disorder. One ...
Sep. 13, 2022 — Researchers report that an experimental drug first developed to treat kidney disease prolongs survival and improves muscle function in mice genetically engineered to develop a severe form of Duchenne ...