Gene Therapy News
May 14, 2024
Top Headlines
Apr. 30, 2024 In an effort to improve delivery of costly medical treatments, a team of researchers in electrical engineering has developed a stimulating method that could make the human body more receptive to ...
Apr. 24, 2024 In a proof-of-concept study, researchers demonstrated the effectiveness of a potential new therapy for Timothy syndrome, an often life-threatening and rare genetic disorder that affects a wide range ...
Apr. 16, 2024 A recent breakthrough study has shown potential to improve therapeutic outcomes for patients suffering from lung ...
Apr. 10, 2024 New research sheds light on the significance of the glucocorticoid receptor in drug-resistant prostate cancer, showing that the development of drug resistance could be prevented by limiting the activity of coregulator ...
Latest Headlines
updated 9:47pm EDT
Apr. 22, 2024 Clarifying the cause of a skin disease led to the discovery of a new disease-causing gene, a new category of diseases, and new perspectives for both counseling and therapy. The discovery is the first ...
Apr. 4, 2024 Researchers have succeeded in correcting a gene defect that causes a hereditary liver disease and its adverse effects on ...
Mar. 21, 2024 Researchers have discovered that a specific mutation in the cancer cells of an aggressive type of blood cancer can prevent novel immunotherapies such as CAR T-cell therapy from working. Their study ...
Mar. 6, 2024 A specific gene may play a key role in new treatments that prevent muscle in the body from breaking down in serious muscle diseases, muscular ...
Mar. 5, 2024 Researchers who work with tiny drug carriers known as lipid nanoparticles have developed a new type of material capable of reaching the lungs and the ...
Mar. 4, 2024 In a discovery that opens the door to a less invasive way of treating some serious disorders before birth, UC San Francisco scientists have found that delivering medicine through amniotic fluid is as ...
Feb. 23, 2024 A new study identified a set of 140 genes that may help predict enhanced disease-free survival in patients with non-small cell lung cancer (NSCLC) ...
Feb. 2, 2024 A group of patients with a hereditary disorder have had their lives transformed by a single treatment of a breakthrough gene-editing therapy, according to the lead ...
Jan. 17, 2024 Axi-cel CAR T targets the CD19 molecule on large B-cell lymphoma cells. The ZUMA-7 trial demonstrated that axi-cel reduced the risk of disease ...
Jan. 2, 2024 Just like a doctor adjusts the dose of a medication to the patient's needs, the expression of therapeutic genes, those modified in a person to treat ...
Earlier Headlines
Dec. 13, 2023 A previously mysterious small RNA molecule in mice is found to play a crucial role in gene expression, and may be the first identified member of a new class of regulatory ...
Dec. 7, 2023 Researchers have laid the foundation for the development of a gene therapy for the genetic heart disease arrhythmogenic cardiomyopathy (ACM). Their approach, based on replacement of the PKP2 gene, ...
Nov. 22, 2023 Leukemia is the most common type of cancer in children. Treatment involves intensive chemotherapy, which has severe side effects due to its non-specific mode of action. A team has now discovered a ...
Nov. 16, 2023 Researchers have discovered that 'cell competition' following gene therapy results in the accumulation of stem cells with genetic mutations which make them grow faster. Some of these ...
Nov. 1, 2023 Many hidden genetic variations can be detected with Chameleolyser, a new method. The information is already yielding new patient diagnoses and may also lead to the discovery of as yet unknown disease ...
Oct. 31, 2023 Individuals living with severe sickle cell disease (SCD) are highly interested in new, potentially curative gene therapy treatments and are willing to accept associated risks for a chance at a cure, ...
Oct. 24, 2023 One problem in gene therapy is that not all genes transfer equally well into the target cells. Researchers have now developed a flexible method to transfer large genes efficiently and without ...
Aug. 30, 2023 A clinical trial has tested a potentially curative stem cell gene therapy for sickle cell disease. The results were ...
Aug. 11, 2023 Researchers have developed a new form of gene therapy that can stop cell division in fusion-driven ...
Aug. 10, 2023 A change in just one letter in the code that makes up a cancer-causing gene can significantly affect how aggressive a tumor is or how well a patient with cancer responds to a particular therapy. A ...
Aug. 10, 2023 Researchers have made a remarkable step forward in finding a potential cure for a type of childhood kidney ...
Aug. 10, 2023 New research has successfully reversed hearing loss in mice. Scientists used a genetic approach to fix deafness in mice, restoring their hearing abilities in low and middle frequency ...
Aug. 9, 2023 A study shows new steps toward more patients getting gene ...
July 27, 2023 In a step forward in the development of genetic medicines, researchers have developed a proof-of-concept model for delivering gene editing tools to treat blood disorders, allowing for the ...
July 12, 2023 Cancer therapies that target specific genetic abnormalities in tumors have revolutionized treatment possibilities over the past two decades. While quality of life and survival are improved with ...
May 30, 2023 A scientific team has designed a strategy to fight obesity and diabetes in mice through ex vivo gene therapy which consists of implanting cells that have been manipulated and transformed in order to ...
Apr. 4, 2023 Researchers uncover a mechanism in a retinal transporter protein that causes blindness, could lead to targeted ...
Feb. 17, 2023 Researchers used the drug fasudil to restore neurons and improve methamphetamine-induced cognitive dysfunction in a mouse model of ...
Jan. 24, 2023 Researchers have uncovered a gene that is overexpressed in mutated IDH1. Studies in human cells and a novel mouse model both show that this gene, called ZMYND8, plays a critical role in the radiation ...
Jan. 11, 2023 Scientists have demonstrated in animal models the possibility of using lipid nanoparticles and messenger RNA, the technology underpinning COVID-19 vaccines, to treat blindness associated with a rare ...
Wednesday, December 13, 2023
Thursday, December 7, 2023
Wednesday, November 22, 2023
Thursday, November 16, 2023
Wednesday, November 1, 2023
Tuesday, October 31, 2023
Tuesday, October 24, 2023
Wednesday, August 30, 2023
Friday, August 11, 2023
Thursday, August 10, 2023
- New Gene Editing Tool Helps Zero in on Small Cancer-Linked Mutations
- Gene Therapy Hope for Children With Kidney Disease
- Scientists Reverse Hearing Loss in Mice
Wednesday, August 9, 2023
Thursday, July 27, 2023
Wednesday, July 12, 2023
Tuesday, May 30, 2023
Tuesday, April 4, 2023
Friday, February 17, 2023
Tuesday, January 24, 2023
Wednesday, January 11, 2023
Wednesday, December 7, 2022
Wednesday, November 9, 2022
Thursday, November 3, 2022
Wednesday, October 26, 2022
Thursday, October 20, 2022
Wednesday, October 19, 2022
Tuesday, October 11, 2022
Monday, October 10, 2022
Friday, September 23, 2022
Wednesday, August 24, 2022
Monday, June 6, 2022
Tuesday, May 10, 2022
Friday, April 22, 2022
Tuesday, April 5, 2022
Friday, April 1, 2022
Tuesday, March 29, 2022
Monday, February 28, 2022
Wednesday, February 16, 2022
Monday, January 24, 2022
Wednesday, January 19, 2022
- Calcium: Important Not Just for Your Bones but Also for Your Heart
- Epilepsy Research Boosts Case for New Gene Therapy for Dravet Syndrome
Tuesday, January 4, 2022
Monday, December 13, 2021
- Experimental Gene Therapy Reverses Sickle Cell Disease for Years
- Gene Network Changes Associated With Cancer Onset and Progression Identify New Treatment Targets